Risdiplam Granted With EMA’s PRIME Designation & Letting Children With SMA Have Big Dreams

Feb 20, 2019, 12:00 AM

SMA News Today’s Director of Multichannel Content, Michael Morale, discusses how Risdiplam was granted the EMA’s PRIME designation for potential in SMA. Also, Community Editor Kevin Schaefer reads from his latest column, in which he encourages parents to let their children with SMA have big dreams.

Are you interested in understanding gene therapy? ExploreGeneTherapy.com has helpful information about gene therapy, including its history and how it is being investigated for the treatment of genetic diseases. Visit www.exploregenetherapy.com

SMA News Today’s Director of Multichannel Content, Michael Morale, discusses how Risdiplam was granted the EMA’s PRIME designation for potential in SMA. Also, Community Editor Kevin Schaefer reads from his latest column, in which he encourages parents to let their children with SMA have big dreams. Are you interested in understanding gene therapy? ExploreGeneTherapy.com has helpful information about gene therapy, including its history and how it is being investigated for the treatment of genetic diseases. Visit www.exploregenetherapy.com